The United States Food and Drug Administration has just approved the first-ever clinical trial that uses CRISPR-Cas13 RNA editing. Its aim is to treat an eye disease called wet age-related macular degeneration that causes vision loss in millions of older people worldwide.
This trial marks a new frontier in gene therapy —the process of treating or curing medical conditions by changing a person’s genes.
What makes it special is the fact the therapy targets RNA, instead of DNA. So, what does that mean, and why should we be excited?
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